Large1 gene transfer in older myd mice with severe muscular dystrophy restores muscle function and greatly improves survival Article

Yonekawa, Takahiro, Rauckhorst, Adam J, El-Hattab, Sara et al. (2022). Large1 gene transfer in older myd mice with severe muscular dystrophy restores muscle function and greatly improves survival . SCIENCE ADVANCES, 8(21), 10.1126/sciadv.abn0379

Open Access

cited authors

  • Yonekawa, Takahiro; Rauckhorst, Adam J; El-Hattab, Sara; Cuellar, Marco A; Venzke, David; Anderson, Mary E; Okuma, Hidehiko; Pewa, Alvin D; Taylor, Eric B; Campbell, Kevin P

sustainable development goals

authors

publication date

  • May 27, 2022

published in

keywords

  • ALPHA-DYSTROGLYCAN
  • COMPLEX
  • DEFECTS
  • DELIVERY
  • GLYCOSYLATION
  • LIFE-SPAN
  • MUTATIONS
  • MYODYSTROPHY
  • Multidisciplinary Sciences
  • SKELETAL
  • Science & Technology
  • Science & Technology - Other Topics
  • THERAPY

Digital Object Identifier (DOI)

publisher

  • AMER ASSOC ADVANCEMENT SCIENCE

volume

  • 8

issue

  • 21