Large1 Gene Transfer in Older myd Mice with Severe Muscular Dystrophy Restores Muscle Function and Greatly Improves Survival Preprint

Yonekawa, Takahiro, Rauckhorst, Adam J, El-Hattab, Sara et al. Large1 Gene Transfer in Older myd Mice with Severe Muscular Dystrophy Restores Muscle Function and Greatly Improves Survival . 10.1101/2021.10.28.466309

cited authors

  • Yonekawa, Takahiro; Rauckhorst, Adam J; El-Hattab, Sara; Cuellar, Marco A; Venzke, David; Anderson, Mary E; Okuma, Hidehiko; Pewa, Alvin D; Taylor, Eric B; Campbell, Kevin P

authors

keywords

  • 2.1 Biological and endogenous factors
  • 32 Biomedical and Clinical Sciences
  • 3208 Medical Physiology
  • 5.1 Pharmaceuticals
  • Biotechnology
  • Brain Disorders
  • Congenital Muscular Dystrophy
  • Congenital Structural Anomalies
  • Duchenne/ Becker Muscular Dystrophy
  • Gene Therapy
  • Genetics
  • Intellectual and Developmental Disabilities (IDD)
  • Muscular Dystrophy
  • Musculoskeletal
  • Neurosciences
  • Orphan Drug
  • Pediatric Research Initiative
  • Rare Diseases

Digital Object Identifier (DOI)